EUS or percutaneously guided intratumoral TNFerade biologic with 5-fluorouracil and radiotherapy for first-line treatment of locally advanced pancreatic cancer: a phase I/II study

Gastrointest Endosc. 2012 Feb;75(2):332-8. doi: 10.1016/j.gie.2011.10.007.

Abstract

Background: TNFeradeBiologic (AdGVEGR.TNF.11D) is a replication-deficient adenoviral vector that expresses tumor necrosis factor-α (TNF-α) under the control of the Egr-1 promoter, which is inducible by chemotherapy and radiation.

Objective: This study was conducted to determine the maximal tolerated dose of TNFeradeBiologic with standard chemoradiotherapy and preliminary activity and safety of the combination in the treatment of locally advanced pancreatic cancer (LAPC).

Design: TNFeradeBiologic was injected into locally advanced pancreatic carcinomas by using EUS or percutaneous administration once a week for 5 weeks together with 50.4 Gy radiation and 5-fluorouracil (5-FU) 200 mg/m(2) daily over 5.5 weeks. Dose levels from 4 × 10(9) to 1 × 10(12) particle units (PU) were studied.

Setting: Multicentered, academic institutions.

Patients: Fifty patients with LAPC were treated.

Interventions: Doses of TNFerade Biologic were administered to patients.

Main outcome measurements: Toleration of TNFerade Biologic was measured through toxicity and tumor response, by using the criteria of the Response Evaluation Criteria in Solid Tumors and the World Health Organization, and was reviewed by a central radiology facility. Overall survival and progression-free survival were also measured.

Results: Dose-limiting toxicities of pancreatitis and cholangitis were observed in 3 patients at the 1 × 10(12) PU dose, making 4 × 10(11) PU the maximum tolerated dose. One complete response, 3 partial responses, and 12 patients with stable disease were noted. Seven patients eventually went to surgery, 6 had clear margins, and 3 survived >24 months.

Limitations: This is a Phase 1/2 non-randomized study.

Conclusions: Intratumoral delivery of TNFerade Biologic by EUS with fine-needle viral injection or percutaneously, combined with chemoradiation, shows promise in the treatment of LAPC. There appeared to be better clinical outcome at the maximal tolerated dose than at lower doses. The dose of 4 ×10(11) PU TNFerade Biologic was generally well tolerated, with encouraging indications of activity, and will be tested in the randomized phase of this study. Delivery of TNFerade Biologic did not interfere with subsequent surgical resection.

Publication types

  • Clinical Trial, Phase I
  • Clinical Trial, Phase II
  • Multicenter Study

MeSH terms

  • Adenoviruses, Human / genetics
  • Adult
  • Aged
  • Antimetabolites, Antineoplastic / therapeutic use
  • Carcinoma / pathology
  • Carcinoma / therapy*
  • Chemoradiotherapy / adverse effects
  • Cholangitis / etiology
  • DNA / administration & dosage
  • DNA / adverse effects
  • DNA / therapeutic use*
  • Disease-Free Survival
  • Dose Fractionation, Radiation
  • Female
  • Fluorouracil / therapeutic use
  • Genetic Vectors / administration & dosage*
  • Genetic Vectors / adverse effects
  • Genetic Vectors / therapeutic use
  • Humans
  • Injections, Intralesional
  • Male
  • Maximum Tolerated Dose*
  • Middle Aged
  • Pancreatic Neoplasms / pathology
  • Pancreatic Neoplasms / therapy*
  • Pancreatitis / etiology
  • Treatment Outcome
  • Tumor Necrosis Factor-alpha / administration & dosage*
  • Tumor Necrosis Factor-alpha / adverse effects
  • Tumor Necrosis Factor-alpha / therapeutic use

Substances

  • Antimetabolites, Antineoplastic
  • TNFeraseBiologic
  • Tumor Necrosis Factor-alpha
  • DNA
  • Fluorouracil